The regions analyzed for the market include North America, Europe, South America, Asia Pacific, the Middle East, and Africa. The North American region emerged as the largest global haemophilia gene therapy market, with a 43.31% market revenue share in 2022. The presence of a significant population suffering from haemophilia is one of the primary drivers of the market. The well-established healthcare infrastructure with an advanced and extensive diagnostics network enables early identification of haemophilia, and further treatments are offered as quickly. The rising prevalence of the condition in the middle-aged group will also aid market growth. The well-established paediatric care is a significant secondary driver that facilitates early detection and treatment of haemophilia in babies. Large pharmaceutical and biotechnology companies are driven by research and development in gene therapies. A strong scientific community with a robust research infrastructure have led to several scientific breakthroughs that have paved the way for harnessing the potential of gene therapies in treating several inherited conditions, including haemophilia. The wide network of insurance coverage and government healthcare packages supports the market's growth.
North America Region Haemophilia Gene Therapy Market Share in 2022 - 43.31%
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The indication segment is divided into haemophilia A and haemophilia B. The haemophilia A segment dominated the market with a market share of around 75% in 2022. Haemophilia A is a bleeding disorder caused due to the absence of factor VII in the baby's genes. It is also known as classic haemophilia. Factor gene plays a significant role in blood clotting. Males are more susceptible to this genetic disorder. For instance, there were 400 babies born in the U.S. with haemophilia A in 2021. Similar statistics are present globally. The lack of proper healthcare infrastructure in low-and-middle-income countries leads to insufficient or no data/statistics on this condition. Haemophilia is expected to dominate the market, given its significant prevalence worldwide.
1. Introduction
1.1. Objectives of the Study
1.2. Market Definition
1.3. Research Scope
1.4. Currency
1.5. Key Target Audience
2. Research Methodology and Assumptions
3. Executive Summary
4. Premium Insights
4.1. Porter’s Five Forces Analysis
4.2. Value Chain Analysis
4.3. Top Investment Pockets
4.3.1. Market Attractiveness Analysis By Indication
4.3.2. Market Attractiveness Analysis By Region
4.4. Industry Trends
5. Market Dynamics
5.1. Market Evaluation
5.2. Drivers
5.2.1. The rising prevalence of haemophilia
5.3. Restraints
5.3.1. Haemophilia gene therapy is expensive
5.4. Opportunities
5.4.1. Growing research and development in gene therapy
5.5. Challenges
5.5.1. Lack of awareness
6. Global Haemophilia Gene Therapy Market Analysis and Forecast, By Indication
6.1. Segment Overview
6.2. Haemophilia A
6.3. Haemophilia B
7. Global Haemophilia Gene Therapy Market Analysis and Forecast, By Regional Analysis
7.1. Segment Overview
7.2. North America
7.2.1. U.S.
7.2.2. Canada
7.2.3. Mexico
7.3. Europe
7.3.1. Germany
7.3.2. France
7.3.3. U.K.
7.3.4. Italy
7.3.5. Spain
7.4. Asia-Pacific
7.4.1. Japan
7.4.2. China
7.4.3. India
7.5. South America
7.5.1. Brazil
7.6. Middle East and Africa
7.6.1. UAE
7.6.2. South Africa
8. Global Haemophilia Gene Therapy Market-Competitive Landscape
8.1. Overview
8.2. Market Share of Key Players in the Haemophilia Gene Therapy Market
8.2.1. Global Company Market Share
8.2.2. North America Company Market Share
8.2.3. Europe Company Market Share
8.2.4. APAC Company Market Share
8.3. Competitive Situations and Trends
8.3.1. Product Launches and Developments
8.3.2. Partnerships, Collaborations, and Agreements
8.3.3. Mergers & Acquisitions
8.3.4. Expansions
9. Company Profiles
9.1. BioMarin Pharmaceuticals Inc.
9.1.1. Business Overview
9.1.2. Company Snapshot
9.1.3. Company Market Share Analysis
9.1.4. Company Product Portfolio
9.1.5. Recent Developments
9.1.6. SWOT Analysis
9.2. F Hoffmann-La Roche
9.2.1. Business Overview
9.2.2. Company Snapshot
9.2.3. Company Market Share Analysis
9.2.4. Company Product Portfolio
9.2.5. Recent Developments
9.2.6. SWOT Analysis
9.3. Freeline Therapeutics
9.3.1. Business Overview
9.3.2. Company Snapshot
9.3.3. Company Market Share Analysis
9.3.4. Company Product Portfolio
9.3.5. Recent Developments
9.3.6. SWOT Analysis
9.4. Pfizer
9.4.1. Business Overview
9.4.2. Company Snapshot
9.4.3. Company Market Share Analysis
9.4.4. Company Product Portfolio
9.4.5. Recent Developments
9.4.6. SWOT Analysis
9.5. Sangamo Therapeutics Inc.
9.5.1. Business Overview
9.5.2. Company Snapshot
9.5.3. Company Market Share Analysis
9.5.4. Company Product Portfolio
9.5.5. Recent Developments
9.5.6. SWOT Analysis
9.6. Shire PLC
9.6.1. Business Overview
9.6.2. Company Snapshot
9.6.3. Company Market Share Analysis
9.6.4. Company Product Portfolio
9.6.5. Recent Developments
9.6.6. SWOT Analysis
9.7. Spark Therapeutics
9.7.1. Business Overview
9.7.2. Company Snapshot
9.7.3. Company Market Share Analysis
9.7.4. Company Product Portfolio
9.7.5. Recent Developments
9.7.6. SWOT Analysis
9.8. Ultragenyx Pharmaceuticals
9.8.1. Business Overview
9.8.2. Company Snapshot
9.8.3. Company Market Share Analysis
9.8.4. Company Product Portfolio
9.8.5. Recent Developments
9.8.6. SWOT Analysis
9.9. uniQure NV
9.9.1. Business Overview
9.9.2. Company Snapshot
9.9.3. Company Market Share Analysis
9.9.4. Company Product Portfolio
9.9.5. Recent Developments
9.9.6. SWOT Analysis
9.10. Zoetis
9.10.1. Business Overview
9.10.2. Company Snapshot
9.10.3. Company Market Share Analysis
9.10.4. Company Component Portfolio
9.10.5. Recent Developments
9.10.6. SWOT Analysis
List of Table
1. Global Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
2. Global Haemophilia A Haemophilia Gene Therapy Market, By Region, 2019-2030 (USD Million)
3. Global Haemophilia B Haemophilia Gene Therapy Market, By Region, 2019-2030 (USD Million)
4. Global Haemophilia Gene Therapy Market, By Region, 2019-2030 (USD Million)
5. North America Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
6. U.S. Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
7. Canada Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
8. Mexico Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
9. Europe Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
10. Germany Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
11. France Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
12. U.K. Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
13. Italy Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
14. Spain Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
15. Asia Pacific Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
16. Japan Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
17. China Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
18. India Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
19. South America Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
20. Brazil Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
21. Middle East and Africa Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
22. UAE Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
23. South Africa Haemophilia Gene Therapy Market, By Indication, 2019-2030 (USD Million)
List of Figures
1. Global Haemophilia Gene Therapy Market Segmentation
2. Haemophilia Gene Therapy Market: Research Methodology
3. Market Size Estimation Methodology: Bottom-Up Approach
4. Market Size Estimation Methodology: Top-Down Approach
5. Data Triangulation
6. Porter’s Five Forces Analysis
7. Value Chain Analysis
8. Global Haemophilia Gene Therapy Market Attractiveness Analysis By Indication
9. Global Haemophilia Gene Therapy Market Attractiveness Analysis By Region
10. Global Haemophilia Gene Therapy Market: Dynamics
11. Global Haemophilia Gene Therapy Market Share by Indication (2022 & 2030)
12. Global Haemophilia Gene Therapy Market Share by Regions (2022 & 2030)
13. Global Haemophilia Gene Therapy Market Share by Company (2021)
This study forecasts revenue at global, regional, and country levels from 2019 to 2030. The Brainy Insights has segmented the haemophilia Gene Therapy market based on below mentioned segments:
Haemophilia Gene Therapy Market by Indication:
Haemophilia Gene Therapy Market by Region:
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